The New England Journal of Medicine has published a study on the long-term efficacy of AAV8-mediated gene therapy (GNT0003) in patients with Crigler-Najjar syndrome, an extremely rare congenital liver disorder affecting approximately 500 people in Europe. It is caused by a deficiency of UGT1A1, an enzyme required for bilirubin metabolism. The accumulation of this substance can lead to…
The proposed changes, estimated to save $320 million, include reversals of Biden-era requirements for hospital emergency departments related to obstetric care.
He said the Tumaini trial is designed to evaluate multiple vaccine candidates through a ring-vaccination approach involving contacts of people confirmed to have Bundibugyo virus disease.
Readers respond to an article by John Harris on the rise in the number of people labelled autistic over the last 20 years John Harris’s article addresses all the main issues that are being debated…