{
  "id": 8083145,
  "title": "FDA approves Ultragenyx's gene therapy for Sanfilippo syndrome type A",
  "url": "https://urgent.news/2026/09/17/fda-approves-ultragenyxs-gene-therapy-for-sanfilippo-syndrome-type-a",
  "topic": "health",
  "section": "Health & Medicine",
  "published": "2026-09-17T19:04:26.000Z",
  "source": {
    "name": "Endpoints News",
    "slug": "endpoints-news",
    "url": "https://endpoints.news/fda-approves-ultragenyxs-gene-therapy-for-sanfilippo-syndrome-type-a/"
  },
  "original_language": "en",
  "account": null,
  "summary": "The FDA granted accelerated approval to a rare disease gene therapy from Ultragenyx on Thursday, giving the company a much-needed boost in an otherwise difficult year. The therapy, called UX111, will be branded as Fayuvi ...",
  "key_points": [],
  "editors_take": null,
  "illustration": null,
  "coverage": {
    "outlets": 2,
    "also_reported_by": [
      {
        "outlet": "STAT News",
        "title": "STAT+: FDA approves a new gene therapy for Sanfilippo syndrome, an ultra-rare disease",
        "url": "https://urgent.news/2026/09/17/stat-fda-approves-a-new-gene-therapy-for-sanfilippo-syndrome-an-ultra",
        "published": "2026-09-17T19:55:46.000Z"
      }
    ]
  },
  "ai_generated": true,
  "disclaimer": "Summaries, key points and the editor’s take are written by software from other outlets’ reporting and may contain errors — always check the linked original."
}